Latest Rare Disease News News
SpringWorks Therapeutics Reports First Quarter 2024
– Achieved $21.0 million in OGSIVEO® (nirogacestat) net product revenue in the…
SpringWorks Therapeutics Reports First Quarter 2024 Financial Results and Highlights Recent Business Updates
– Initiated rolling submission of NDA to the FDA for mirdametinib for…
Aplastic Anemia Market Forecast 2034: FDA, EMA, PDMA Approvals, Clinical Trials, Epidemiology, Therapies … – Barchart
Aplastic Anemia Market Forecast 2034: FDA, EMA, PDMA Approvals, Clinical Trials, Epidemiology,…
Before The 90 Days Season 4?
Summary Stephanie Matto faced relationship challenges on 90 Day Fiancé with Erika…
$2.7 million grant to explore hypoxia’s impac
image: Ngoc Tung Tran, PhD and Reuben Kapur, PhD view more Credit: Indiana…
Anjali Sharathkumar, MD, Shares Romiplostim Outcomes in Severe Aplastic Anemia With MDS – DocWire News
Anjali Sharathkumar, MD, Shares Romiplostim Outcomes in Severe Aplastic Anemia With MDS DocWire…
Anlotinib Enhances Desmoid Fibromatosis Control in New Study
Surgery plus anlotinib as a treatment regimen for desmoid fibromatosis (DF), an…
ChemoCentryx’s Avacopan Scores European Approval For ANCA
The European Union has approved ChemoCentryx Inc's (NASDAQ: CCXI) Tavneos (avacopan) for…
SpringWorks Therapeutics Announces Abstracts Accepted for
– Results from Phase 2b ReNeu trial of mirdametinib in NF1-PN accepted…